Advanced Pharmacy and Clinical Research

Clinical Trials for Rare Diseases

Clinical trials for rare diseases, also known as orphan diseases, present unique challenges and opportunities in the field of medical research. Rare diseases are defined as conditions that affect a small percentage of the population, typically fewer than 1 in 2,000 people. Due to their rarity, these diseases often have limited research and treatment options. Clinical trials for rare diseases are crucial for advancing understanding and developing therapies.